[1] Hadassah Hebrew Univ Hosp, Agnes Ginges Ctr Human Neurogenet, Dept Neurol, IL-91120 Jerusalem, Israel
[2] Univ Rochester, Med Ctr, Dept Neurol, Div Cell & Gene Therapy, Rochester, NY 14642 USA
[3] Univ Rochester, Med Ctr, Dept Neurosurg, Div Cell & Gene Therapy, Rochester, NY 14642 USA