194th ENMC international workshop. 3rd ENMC workshop on exon skipping: Towards clinical application of antisense-mediated exon skipping for Duchenne muscular dystrophy 8-10 December 2012, Naarden, The Netherlands

被引：14

作者：

Aartsma-Rus, Annemieke ^{[1
]}

Muntoni, Francesco ^{[2
,3
]}

机构：

[1] Leiden Univ, Med Ctr, Dept Human Genet, NL-2333 ZA Leiden, Netherlands

[2] Inst Child Hlth, Dubowitz Neuromuscular Ctr, London WC1N 1EH, England

[3] Great Ormond St Hosp Sick Children, London WC1N 1EH, England

来源：

NEUROMUSCULAR DISORDERS | 2013年 / 23卷 / 11期

基金：

英国医学研究理事会;

关键词：

CARDIAC-MUSCLE; RESTORATION; EXPRESSION;

D O I：

10.1016/j.nmd.2013.06.369

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

[No abstract available]

引用

页码：934 / 944

页数：11

共 30 条

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