MEDICINE Sickle Cell Disease at 100 Years

被引：30

作者：

Orkin, Stuart H. ^{[1
,2
]}

Higgs, Douglas R. ^{[3
]}

机构：

[1] Childrens Hosp, Boston, MA 02115 USA

[2] Harvard Univ, Sch Med, Howard Hughes Med Inst, Dana Farber Canc Inst, Boston, MA 02115 USA

[3] John Radcliffe Hosp, Weatherall Inst Mol Med, Oxford 0X3 9DS, England

来源：

SCIENCE | 2010年 / 329卷 / 5989期

关键词：

FETAL-HEMOGLOBIN; BETA-THALASSEMIA; RISK-FACTORS; ANEMIA; BCL11A; EXPRESSION; BURDEN;

D O I：

10.1126/science.1194035

中图分类号：

O [数理科学和化学]; P [天文学、地球科学]; Q [生物科学]; N [自然科学总论];

学科分类号：

07 ; 0710 ; 09 ;

摘要：

Effective strategies to treat sickle cell disease could involve manipulating the type of hemoglobin produced in patients.

引用

页码：291 / 292

页数：2

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