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Adeno-associated virus vectors in clinical trials
被引:137
作者
:
Carter, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
Targeted Genet Corp, Seattle, WA 98101 USA
Targeted Genet Corp, Seattle, WA 98101 USA
Carter, BJ
[
1
]
机构
:
[1]
Targeted Genet Corp, Seattle, WA 98101 USA
来源
:
HUMAN GENE THERAPY
|
2005年
/ 16卷
/ 05期
关键词
:
D O I
:
10.1089/hum.2005.16.541
中图分类号
:
Q81 [生物工程学(生物技术)];
Q93 [微生物学];
学科分类号
:
071005 ;
0836 ;
090102 ;
100705 ;
摘要
:
[No abstract available]
引用
收藏
页码:541 / 550
页数:10
相关论文
共 63 条
[1]
In vivo model of adeno-associated virus vector persistence and rescue
Afione, SA
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Afione, SA
Conrad, CK
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Conrad, CK
Kearns, WG
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Kearns, WG
Chunduru, S
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Chunduru, S
Adams, R
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Adams, R
Reynolds, TC
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Reynolds, TC
Guggino, WB
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Guggino, WB
Cutting, GR
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Cutting, GR
Carter, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Carter, BJ
Flotte, TR
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Flotte, TR
[J].
JOURNAL OF VIROLOGY,
1996,
70
(05)
: 3235
-
3241
[2]
A phase I study of aerosolized administration of tgAAVCF to cystic fibrosis subjects with mild lung disease
Aitken, ML
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Aitken, ML
Moss, RB
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Moss, RB
Waltz, DA
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Waltz, DA
Dovey, ME
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Dovey, ME
Tonelli, MR
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Tonelli, MR
McNamara, SC
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
McNamara, SC
Gibson, RL
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Gibson, RL
Ramsey, BW
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Ramsey, BW
Carter, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Carter, BJ
Reynolds, TC
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Reynolds, TC
[J].
HUMAN GENE THERAPY,
2001,
12
(15)
: 1907
-
1916
[3]
AMINOFF M, 2004, MIN NIH REC DNA ADV
[4]
Arruda VR, 2003, MOL THER, V7, pS161
[5]
Lack of germline transmission of vector sequences following systemic administration of recombinant AAV-2 vector in males
Arruda, VR
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Arruda, VR
Fields, PA
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Fields, PA
Milner, R
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Milner, R
Wainwright, L
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Wainwright, L
De Miguel, MP
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
De Miguel, MP
Donovan, PJ
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Donovan, PJ
Herzog, RW
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Herzog, RW
Nichols, TC
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Nichols, TC
Biegel, JA
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Biegel, JA
Razavi, M
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Razavi, M
Dake, M
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Dake, M
Huff, D
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Huff, D
Flake, AW
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Flake, AW
Couto, L
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Couto, L
Kay, MA
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Kay, MA
High, KA
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
High, KA
[J].
MOLECULAR THERAPY,
2001,
4
(06)
: 586
-
592
[6]
Repeated delivery of adeno-associated virus vectors to the rabbit airway
Beck, SE
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Beck, SE
Jones, LA
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Jones, LA
Chesnut, K
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Chesnut, K
Walsh, SM
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Walsh, SM
Reynolds, TC
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Reynolds, TC
Carter, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Carter, BJ
Askin, FB
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Askin, FB
Flotte, TR
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Flotte, TR
Guggino, WB
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Guggino, WB
[J].
JOURNAL OF VIROLOGY,
1999,
73
(11)
: 9446
-
9455
[7]
BENNETT DA, 2004, MIN NIH REC DNA ADV
[8]
BLACKLOW N R, 1988, P165
[9]
Adeno-associated virus and the development of adeno-associated virus vectors: A historical perspective
Carter, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
Targeted Genet Corp, Seattle, WA 98101 USA
Targeted Genet Corp, Seattle, WA 98101 USA
Carter, BJ
[J].
MOLECULAR THERAPY,
2004,
10
(06)
: 981
-
989
[10]
CARTER BJ, 2004, GENE CELL THERAPY TH, P53
←
1
2
3
4
5
6
7
→
共 63 条
[1]
In vivo model of adeno-associated virus vector persistence and rescue
Afione, SA
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Afione, SA
Conrad, CK
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Conrad, CK
Kearns, WG
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Kearns, WG
Chunduru, S
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Chunduru, S
Adams, R
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Adams, R
Reynolds, TC
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Reynolds, TC
Guggino, WB
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Guggino, WB
Cutting, GR
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Cutting, GR
Carter, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Carter, BJ
Flotte, TR
论文数:
0
引用数:
0
h-index:
0
机构:
JOHNS HOPKINS UNIV, SCH MED, DEPT PHYSIOL, BALTIMORE, MD USA
Flotte, TR
[J].
JOURNAL OF VIROLOGY,
1996,
70
(05)
: 3235
-
3241
[2]
A phase I study of aerosolized administration of tgAAVCF to cystic fibrosis subjects with mild lung disease
Aitken, ML
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Aitken, ML
Moss, RB
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Moss, RB
Waltz, DA
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Waltz, DA
Dovey, ME
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Dovey, ME
Tonelli, MR
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Tonelli, MR
McNamara, SC
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
McNamara, SC
Gibson, RL
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Gibson, RL
Ramsey, BW
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Ramsey, BW
Carter, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Carter, BJ
Reynolds, TC
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Washington, Dept Med & Pediat, Seattle, WA 98195 USA
Reynolds, TC
[J].
HUMAN GENE THERAPY,
2001,
12
(15)
: 1907
-
1916
[3]
AMINOFF M, 2004, MIN NIH REC DNA ADV
[4]
Arruda VR, 2003, MOL THER, V7, pS161
[5]
Lack of germline transmission of vector sequences following systemic administration of recombinant AAV-2 vector in males
Arruda, VR
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Arruda, VR
Fields, PA
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Fields, PA
Milner, R
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Milner, R
Wainwright, L
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Wainwright, L
De Miguel, MP
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
De Miguel, MP
Donovan, PJ
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Donovan, PJ
Herzog, RW
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Herzog, RW
Nichols, TC
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Nichols, TC
Biegel, JA
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Biegel, JA
Razavi, M
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Razavi, M
Dake, M
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Dake, M
Huff, D
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Huff, D
Flake, AW
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Flake, AW
Couto, L
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Couto, L
Kay, MA
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Kay, MA
High, KA
论文数:
0
引用数:
0
h-index:
0
机构:
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
Univ Penn, Childrens Hosp Philadelphia, Sch Med, Philadelphia, PA 19104 USA
High, KA
[J].
MOLECULAR THERAPY,
2001,
4
(06)
: 586
-
592
[6]
Repeated delivery of adeno-associated virus vectors to the rabbit airway
Beck, SE
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Beck, SE
Jones, LA
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Jones, LA
Chesnut, K
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Chesnut, K
Walsh, SM
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Walsh, SM
Reynolds, TC
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Reynolds, TC
Carter, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Carter, BJ
Askin, FB
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Askin, FB
Flotte, TR
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Flotte, TR
Guggino, WB
论文数:
0
引用数:
0
h-index:
0
机构:
Johns Hopkins Univ, Sch Med, Eudowood Div Pediat Resp Sci, Baltimore, MD 21205 USA
Guggino, WB
[J].
JOURNAL OF VIROLOGY,
1999,
73
(11)
: 9446
-
9455
[7]
BENNETT DA, 2004, MIN NIH REC DNA ADV
[8]
BLACKLOW N R, 1988, P165
[9]
Adeno-associated virus and the development of adeno-associated virus vectors: A historical perspective
Carter, BJ
论文数:
0
引用数:
0
h-index:
0
机构:
Targeted Genet Corp, Seattle, WA 98101 USA
Targeted Genet Corp, Seattle, WA 98101 USA
Carter, BJ
[J].
MOLECULAR THERAPY,
2004,
10
(06)
: 981
-
989
[10]
CARTER BJ, 2004, GENE CELL THERAPY TH, P53
←
1
2
3
4
5
6
7
→