Adeno-associated virus vectors in clinical trials

[41] Adeno-associated virus-mediated aspartoacylase gene transfer to the brain of knockout mouse for Canavan disease [J]. MOLECULAR THERAPY, 2003, 7 (05) : 580 - 587

[42] Integration of adeno-associated virus (AAV) and recombinant AAV vectors [J]. ANNUAL REVIEW OF GENETICS, 2004, 38 : 819 - 845

[43] MEASE P, 2003, NIH REC DNA ADV COMM

[44] Repeated adeno-associated virus serotype 2 aerosol-mediated cystic fibrosis transmembrane regulator gene transfer to the lungs of patients with cystic fibrosis - A multicenter, double-blind, placebo-controlled trial [J]. CHEST, 2004, 125 (02) : 509 - 521

[45] Sustained phenotypic correction of hemophilia B dogs with a factor IX null mutation by liver-directed gene therapy [J]. BLOOD, 2002, 99 (08) : 2670 - 2676

[46] Munson KL, 2003, MOL THER, V7, pS267

[47] Role of hepatocyte direct hyperplasia in lentivirus-mediated liver transduction in vivo [J]. HUMAN GENE THERAPY, 2002, 13 (05) : 653 - 663

[48] Secretion of a TNFR:Fc fusion protein following pulmonary administration of pseudotyped adeno-associated virus vectors [J]. JOURNAL OF VIROLOGY, 2004, 78 (22) : 12355 - 12365

[49] Schnepp BC, 2003, MOL THER, V7, pS160

[50] Genetic fate of recombinant adeno-associated virus vector genomes in muscle [J]. JOURNAL OF VIROLOGY, 2003, 77 (06) : 3495 - 3504

[41] Adeno-associated virus-mediated aspartoacylase gene transfer to the brain of knockout mouse for Canavan disease [J]. MOLECULAR THERAPY, 2003, 7 (05) : 580 - 587

[42] Integration of adeno-associated virus (AAV) and recombinant AAV vectors [J]. ANNUAL REVIEW OF GENETICS, 2004, 38 : 819 - 845

[43] MEASE P, 2003, NIH REC DNA ADV COMM

[44] Repeated adeno-associated virus serotype 2 aerosol-mediated cystic fibrosis transmembrane regulator gene transfer to the lungs of patients with cystic fibrosis - A multicenter, double-blind, placebo-controlled trial [J]. CHEST, 2004, 125 (02) : 509 - 521

[45] Sustained phenotypic correction of hemophilia B dogs with a factor IX null mutation by liver-directed gene therapy [J]. BLOOD, 2002, 99 (08) : 2670 - 2676

[46] Munson KL, 2003, MOL THER, V7, pS267

[47] Role of hepatocyte direct hyperplasia in lentivirus-mediated liver transduction in vivo [J]. HUMAN GENE THERAPY, 2002, 13 (05) : 653 - 663

[48] Secretion of a TNFR:Fc fusion protein following pulmonary administration of pseudotyped adeno-associated virus vectors [J]. JOURNAL OF VIROLOGY, 2004, 78 (22) : 12355 - 12365

[49] Schnepp BC, 2003, MOL THER, V7, pS160

[50] Genetic fate of recombinant adeno-associated virus vector genomes in muscle [J]. JOURNAL OF VIROLOGY, 2003, 77 (06) : 3495 - 3504