Gene therapy for hemophilia: hopes and hurdles

被引:14
作者
Chuah, MKL [1 ]
Collen, D [1 ]
VandenDriessche, T [1 ]
机构
[1] Univ Leuven VIB, Ctr Transgene Technol & Gene Therapy, Retroviral Gene Transfer Sect, B-3000 Leuven, Belgium
关键词
D O I
10.1016/S1040-8428(98)00022-5
中图分类号
R73 [肿瘤学];
学科分类号
100214 ;
摘要
[No abstract available]
引用
收藏
页码:153 / 171
页数:19
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共 124 条
[71]  
Liles D, 1997, THROMB HAEMOSTASIS, V77, P944
[72]   A coagulation factor IX-deficient mouse model for human hemophilia B [J].
Lin, HF ;
Maeda, N ;
Smithies, O ;
Straight, DL ;
Stafford, DW .
BLOOD, 1997, 90 (10) :3962-3966
[73]   EXPRESSION OF HUMAN FACTOR-IX BY MICROENCAPSULATED RECOMBINANT FIBROBLASTS [J].
LIU, HW ;
OFOSU, FA ;
CHANG, PL .
HUMAN GENE THERAPY, 1993, 4 (03) :291-301
[74]   Gut epithelial cells as targets for gene therapy of hemophilia [J].
Lozier, JN ;
Yankaskas, JR ;
Ramsey, WJ ;
Chen, L ;
Berschneider, H ;
Morgan, RA .
HUMAN GENE THERAPY, 1997, 8 (12) :1481-1490
[75]   EFFICIENT TRANSFECTION OF PRIMARY-CELLS IN A CANINE HEMOPHILIA-B MODEL USING ADENOVIRUS POLYLYSINE DNA COMPLEXES [J].
LOZIER, JN ;
THOMPSON, AR ;
HU, PC ;
READ, M ;
BRINKHOUS, KM ;
HIGH, KA ;
CURIEL, DT .
HUMAN GENE THERAPY, 1994, 5 (03) :313-322
[76]   GENE-THERAPY AND THE HEMOPHILIAS [J].
LOZIER, JN ;
BRINKHOUS, KM .
JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION, 1994, 271 (01) :47-51
[77]  
LU DR, 1993, SCI CHINA SER B, V36, P1342
[78]   SEQUENCES IN THE CODING REGION OF CLOTTING FACTOR-VIII ACT AS DOMINANT INHIBITORS OF RNA ACCUMULATION AND PROTEIN-PRODUCTION [J].
LYNCH, CM ;
ISRAEL, DI ;
KAUFMAN, RJ ;
MILLER, AD .
HUMAN GENE THERAPY, 1993, 4 (03) :259-272
[79]  
MILLER AD, 1993, METHOD ENZYMOL, V217, P581
[80]  
MILLER AD, 1992, CURR TOP MICROBIOL, V158, P1