Targeted mutagenesis in mice by electroporation of Cpf1 ribonucleoproteins

被引:175
作者
Hur, Junho K. [1 ]
Kim, Kyoungmi [1 ]
Been, Kyung Wook [1 ,2 ]
Baek, Gayoung [1 ]
Ye, Sunghyeok [1 ,3 ]
Hur, Junseok W. [1 ,4 ]
Ryu, Seuk-Min [1 ,2 ]
Lee, Youn Su [1 ,5 ]
Kim, Jin-Soo [1 ,2 ]
机构
[1] Inst for Basic Sci Korea, Ctr Genome Engn, Seoul, South Korea
[2] Seoul Natl Univ, Dept Chem, Seoul, South Korea
[3] Korea Univ Sci & Technol, IBS Sch, Basic Sci, Seoul, South Korea
[4] Korea Univ, Coll Med, Dept Neurosurg, Seoul, South Korea
[5] ToolGen, Seoul, South Korea
关键词
RNA-GUIDED ENDONUCLEASE; HUMAN-CELLS; CAS9;
D O I
10.1038/nbt.3596
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
引用
收藏
页码:807 / 808
页数:2
相关论文
共 10 条
[1]   Heritable Gene Knockout in Caenorhabditis elegans by Direct Injection of Cas9-sgRNA Ribonucleoproteins [J].
Cho, Seung Woo ;
Lee, Jihyun ;
Carroll, Dana ;
Kim, Jin-Soo ;
Lee, Junho .
GENETICS, 2013, 195 (03) :1177-+
[2]   Targeted genome engineering in human cells with the Cas9 RNA-guided endonuclease [J].
Cho, Seung Woo ;
Kim, Sojung ;
Kim, Jong Min ;
Kim, Jin-Soo .
NATURE BIOTECHNOLOGY, 2013, 31 (03) :230-232
[3]   Multiplex Genome Engineering Using CRISPR/Cas Systems [J].
Cong, Le ;
Ran, F. Ann ;
Cox, David ;
Lin, Shuailiang ;
Barretto, Robert ;
Habib, Naomi ;
Hsu, Patrick D. ;
Wu, Xuebing ;
Jiang, Wenyan ;
Marraffini, Luciano A. ;
Zhang, Feng .
SCIENCE, 2013, 339 (6121) :819-823
[4]   A Programmable Dual-RNA-Guided DNA Endonuclease in Adaptive Bacterial Immunity [J].
Jinek, Martin ;
Chylinski, Krzysztof ;
Fonfara, Ines ;
Hauer, Michael ;
Doudna, Jennifer A. ;
Charpentier, Emmanuelle .
SCIENCE, 2012, 337 (6096) :816-821
[5]   Simple Genome Editing of Rodent Intact Embryos by Electroporation [J].
Kaneko, Takehito ;
Mashimo, Tomoji .
PLoS One, 2015, 10 (11)
[6]   Highly efficient RNA-guided genome editing in human cells via delivery of purified Cas9 ribonucleoproteins [J].
Kim, Sojung ;
Kim, Daesik ;
Cho, Seung Woo ;
Kim, Jungeun ;
Kim, Jin-Soo .
GENOME RESEARCH, 2014, 24 (06) :1012-1019
[7]   RNA-Guided Human Genome Engineering via Cas9 [J].
Mali, Prashant ;
Yang, Luhan ;
Esvelt, Kevin M. ;
Aach, John ;
Guell, Marc ;
DiCarlo, James E. ;
Norville, Julie E. ;
Church, George M. .
SCIENCE, 2013, 339 (6121) :823-826
[8]   Homology-directed repair in rodent zygotes using Cas9 and TALEN engineered proteins [J].
Menoret, Severine ;
De Cian, Anne ;
Tesson, Laurent ;
Remy, Severine ;
Usal, Claire ;
Boule, Jean-Baptiste ;
Boix, Charlotte ;
Fontaniere, Sandra ;
Creneguy, Alison ;
Nguyen, Tuan H. ;
Brusselle, Lucas ;
Thinard, Reynald ;
Gauguier, Dominique ;
Concordet, Jean-Paul ;
Cherifi, Yacine ;
Fraichard, Alexandre ;
Giovannangeli, Carine ;
Anegon, Ignacio .
SCIENTIFIC REPORTS, 2015, 5
[9]   DNA-free genome editing in plants with preassembled CRISPR-Cas9 ribonucleoproteins [J].
Woo, Je Wook ;
Kim, Jungeun ;
Kwon, Soon Il ;
Corvalan, Claudia ;
Cho, Seung Woo ;
Kim, Hyeran ;
Kim, Sang-Gyu ;
Kim, Sang-Tae ;
Choe, Sunghwa ;
Kim, Jin-Soo .
NATURE BIOTECHNOLOGY, 2015, 33 (11) :1162-+
[10]   Cpf1 Is a Single RNA-Guided Endonuclease of a Class 2 CRISPR-Cas System [J].
Zetsche, Bernd ;
Gootenberg, Jonathan S. ;
Abudayyeh, Omar O. ;
Slaymaker, Ian M. ;
Makarova, Kira S. ;
Essletzbichler, Patrick ;
Volz, Sara E. ;
Joung, Julia ;
van der Oost, John ;
Regev, Aviv ;
Koonin, Eugene V. ;
Zhang, Feng .
CELL, 2015, 163 (03) :759-771