[1] Univ Penn, Inst Human Gene Therapy, Wistar Inst 204, Philadelphia, PA 19104 USA
[2] Univ Penn, Dept Mol & Cellular Engn, Wistar Inst 204, Philadelphia, PA 19104 USA
[3] Hotel Dieu, INSERM, UMR 533, F-44000 Nantes, France
[4] Univ Oxford, Dept Human Anat & Genet, Oxford OX1 3QU, England