Natural history and treatment of renal involvement in Fabry disease

被引:109
作者
Branton, M
Schiffmann, R
Kopp, JB
机构
[1] NIDDKD, Kidney Dis Sect, NIH, Bethesda, MD 20892 USA
[2] NINCDS, Dev & Metab Neurol Branch, NIH, Bethesda, MD 20892 USA
来源
JOURNAL OF THE AMERICAN SOCIETY OF NEPHROLOGY | 2002年 / 13卷 / 06期
关键词
D O I
10.1097/01.ASN.0000016683.73778.78
中图分类号
R5 [内科学]; R69 [泌尿科学(泌尿生殖系疾病)];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:S139 / S143
页数:5
相关论文
共 13 条
[11]   Enzyme replacement therapy in Fabry disease - A randomized controlled trial [J].
Schiffmann, R ;
Kopp, JB ;
Austin, HA ;
Sabnis, S ;
Moore, DF ;
Weibel, T ;
Balow, JE ;
Brady, RO .
JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION, 2001, 285 (21) :2743-2749
[12]   EARLY RENAL-FAILURE IN FABRYS-DISEASE [J].
SHETH, KJ ;
ROTH, DA ;
ADAMS, MB .
AMERICAN JOURNAL OF KIDNEY DISEASES, 1983, 2 (06) :651-654
[13]   Patients with Fabry disease on dialysis in the United States [J].
Thadhani, R ;
Wolf, M ;
West, ML ;
Tonelli, M ;
Ruthazer, R ;
Pastores, GM ;
Obrador, GT .
KIDNEY INTERNATIONAL, 2002, 61 (01) :249-255