Bad for cats, good for humans? Modified feline immunodeficiency virus for gene therapy

被引:5
作者
Crystal, RG [1 ]
机构
[1] Cornell Univ, Weill Med Coll, Inst Med Genet, New York, NY 10021 USA
关键词
D O I
10.1172/JCI8838
中图分类号
R-3 [医学研究方法]; R3 [基础医学];
学科分类号
1001 ;
摘要
引用
收藏
页码:1491 / 1493
页数:3
相关论文
共 23 条
[1]  
ANDERSON JM, 1995, AM J PHYSIOL, V269, P467
[2]   Aerosol administration of a recombinant adenovirus expressing CFTR to cystic fibrosis patients: A phase I clinical trial [J].
Bellon, G ;
MichelCalemard, L ;
Thouvenot, D ;
Jagneaux, V ;
Poitevin, F ;
Malcus, C ;
Accart, N ;
Layani, MP ;
Aymard, M ;
Bernon, H ;
Bienvenu, J ;
Courtney, M ;
Doring, G ;
Gilly, B ;
Gilly, R ;
Lamy, D ;
Levrey, H ;
Morel, Y ;
Paulin, C ;
Perraud, F ;
Rodillon, L ;
Sene, C ;
So, S ;
TouraineMoulin, F ;
Schatz, C ;
Pavirani, A .
HUMAN GENE THERAPY, 1997, 8 (01) :15-25
[3]   LIPOSOME-MEDIATED CFTR GENE-TRANSFER TO THE NASAL EPITHELIUM OF PATIENTS WITH CYSTIC-FIBROSIS [J].
CAPLEN, NJ ;
ALTON, EWFW ;
MIDDLETON, PG ;
DORIN, JR ;
STEVENSON, BJ ;
GAO, X ;
DURHAM, SR ;
JEFFERY, PK ;
HODSON, ME ;
COUTELLE, C ;
HUANG, L ;
PORTEOUS, DJ ;
WILLIAMSON, R ;
GEDDES, DM .
NATURE MEDICINE, 1995, 1 (01) :39-46
[4]   ADMINISTRATION OF AN ADENOVIRUS CONTAINING THE HUMAN CFTR CDNA TO THE RESPIRATORY-TRACT OF INDIVIDUALS WITH CYSTIC-FIBROSIS [J].
CRYSTAL, RG ;
MCELVANEY, NG ;
ROSENFELD, MA ;
CHU, CS ;
MASTRANGELI, A ;
HAY, JG ;
BRODY, SL ;
JAFFE, HA ;
EISSA, NT ;
DANEL, C .
NATURE GENETICS, 1994, 8 (01) :42-51
[5]   TRANSFER OF GENES TO HUMANS - EARLY LESSONS AND OBSTACLES TO SUCCESS [J].
CRYSTAL, RG .
SCIENCE, 1995, 270 (5235) :404-410
[6]   Molecular structure and assembly of the tight junction [J].
Denker, BM ;
Nigam, SK .
AMERICAN JOURNAL OF PHYSIOLOGY-RENAL PHYSIOLOGY, 1998, 274 (01) :F1-F9
[7]   Circular intermediates of recombinant adeno-associated virus have defined structural characteristics responsible for long-term episomal persistence in muscle tissue [J].
Duan, DS ;
Sharma, P ;
Yang, JS ;
Yue, YP ;
Dudus, L ;
Zhang, YL ;
Fisher, KJ ;
Engelhardt, JF .
JOURNAL OF VIROLOGY, 1998, 72 (11) :8568-8577
[8]   A phase I study of an adeno-associated virus-CFTR gene vector in adult CF patients with mild lung disease [J].
Flotte, T ;
Carter, B ;
Conrad, C ;
Guggino, W ;
Reynolds, T ;
Rosenstein, B ;
Taylor, G ;
Walden, S ;
Wetzel, R .
HUMAN GENE THERAPY, 1996, 7 (09) :1145-1159
[9]   A placebo-controlled study of liposome-mediated gene transfer to the nasal epithelium of patients with cystic fibrosis [J].
Gill, DR ;
Southern, KW ;
Mofford, KA ;
Seddon, T ;
Huang, L ;
Sorgi, F ;
Thomson, A ;
MacVinish, LJ ;
Ratcliff, R ;
Bilton, D ;
Lane, DJ ;
Littlewood, JM ;
Webb, AK ;
Middleton, PG ;
Colledge, WH ;
Cuthbert, AW ;
Evans, MJ ;
Higgins, CF ;
Hyde, SC .
GENE THERAPY, 1997, 4 (03) :199-209
[10]   Lentiviral vectors for gene therapy of cystic fibrosis [J].
Goldman, MJ ;
Lee, PS ;
Yang, JS ;
Wilson, JM .
HUMAN GENE THERAPY, 1997, 8 (18) :2261-2268