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Enzyme-replacement therapy for metabolic storage disorders
被引:73
作者
:
Brady, RO
论文数:
0
引用数:
0
h-index:
0
机构:
NIH, Dev & Metab Neurol Branch, NINDS, Bethesda, MD 20892 USA
NIH, Dev & Metab Neurol Branch, NINDS, Bethesda, MD 20892 USA
Brady, RO
[
1
]
Schiffmann, R
论文数:
0
引用数:
0
h-index:
0
机构:
NIH, Dev & Metab Neurol Branch, NINDS, Bethesda, MD 20892 USA
NIH, Dev & Metab Neurol Branch, NINDS, Bethesda, MD 20892 USA
Schiffmann, R
[
1
]
机构
:
[1]
NIH, Dev & Metab Neurol Branch, NINDS, Bethesda, MD 20892 USA
来源
:
LANCET NEUROLOGY
|
2004年
/ 3卷
/ 12期
关键词
:
D O I
:
10.1016/S1474-4422(04)00938-X
中图分类号
:
R74 [神经病学与精神病学];
学科分类号
:
摘要
:
引用
收藏
页码:752 / 756
页数:5
相关论文
共 36 条
[1]
Recombinant human acid α-glucosidase enzyme therapy for infantile glycogen storage disease type II:: Results of a phase I/II clinical trial
Amalfitano, A
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Amalfitano, A
Bengur, AR
论文数:
0
引用数:
0
h-index:
0
机构:
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Bengur, AR
Morse, RP
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Morse, RP
Majure, JM
论文数:
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h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Majure, JM
Case, LE
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Case, LE
Veerling, DL
论文数:
0
引用数:
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h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Veerling, DL
Mackey, J
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h-index:
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机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Mackey, J
论文数:
引用数:
h-index:
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Kishnani, P
Smith, W
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McVie-Wylie, A
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机构:
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McVie-Wylie, A
Sullivan, JA
论文数:
0
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h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Sullivan, JA
Hoganson, GE
论文数:
0
引用数:
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h-index:
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机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Hoganson, GE
Phillips, JA
论文数:
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机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Phillips, JA
Schaefer, GB
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Charrow, J
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Wiethoff, CM
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Johannes Gutenberg Univ Mainz, Childrens Hosp, D-55101 Mainz, Germany
Johannes Gutenberg Univ Mainz, Childrens Hosp, D-55101 Mainz, Germany
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机构:
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共 36 条
[1]
Recombinant human acid α-glucosidase enzyme therapy for infantile glycogen storage disease type II:: Results of a phase I/II clinical trial
Amalfitano, A
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Amalfitano, A
Bengur, AR
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Bengur, AR
Morse, RP
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Morse, RP
Majure, JM
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Majure, JM
Case, LE
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Case, LE
Veerling, DL
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Veerling, DL
Mackey, J
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0
引用数:
0
h-index:
0
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Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Mackey, J
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Kishnani, P
Smith, W
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0
引用数:
0
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机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Smith, W
McVie-Wylie, A
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0
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0
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0
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Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
McVie-Wylie, A
Sullivan, JA
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0
引用数:
0
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机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Sullivan, JA
Hoganson, GE
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0
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机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Hoganson, GE
Phillips, JA
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引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Phillips, JA
Schaefer, GB
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0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Schaefer, GB
Charrow, J
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0
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0
h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Charrow, J
Ware, RE
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0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Ware, RE
Bossen, EH
论文数:
0
引用数:
0
h-index:
0
机构:
Duke Univ, Med Ctr, Dept Pediat, Durham, NC 27710 USA
Bossen, EH
Chen, YT
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