Adeno-associated virus vectors for therapeutic gene transfer

[11] Expression of human factor VIII by splicing between dimerized AAV vectors [J]. MOLECULAR THERAPY, 2002, 5 (06) : 716 - 722

[12] Sustained and complete phenotype correction of hemophilia B mice following intramuscular injection of AAV1 serotype vectors [J]. MOLECULAR THERAPY, 2001, 4 (03) : 217 - 222

[13] Induction of tolerance to human factor VIII in mice [J]. BLOOD, 2001, 97 (10) : 3311 - 3312

[14] Cloning of adeno-associated virus type 4 (AAV4) and generation of recombinant AAV4 particles [J]. JOURNAL OF VIROLOGY, 1997, 71 (09) : 6823 - 6833

[15] Cloning and characterization of adeno-associated virus type 5 [J]. JOURNAL OF VIROLOGY, 1999, 73 (02) : 1309 - 1319

[16] Conrad CK, 1996, GENE THER, V3, P658

[17] Recombinant adeno-associated virus type 2, 4, and 5 vectors: Transduction of variant cell types and regions in the mammalian central nervous system [J]. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 2000, 97 (07) : 3428 - 3432

[18] A new dual-vector approach to enhance recombinant adeno-associated virus-mediated gene expression through intermolecular cis activation [J]. NATURE MEDICINE, 2000, 6 (05) : 595 - 598

[19] Enhancement of muscle gene delivery with pseudotyped adeno-associated virus type 5 correlates with myoblast differentiation [J]. JOURNAL OF VIROLOGY, 2001, 75 (16) : 7662 - 7671

[20] Structural analysis of adeno-associated virus transduction circular intermediates [J]. VIROLOGY, 1999, 261 (01) : 8 - 14

[11] Expression of human factor VIII by splicing between dimerized AAV vectors [J]. MOLECULAR THERAPY, 2002, 5 (06) : 716 - 722

[12] Sustained and complete phenotype correction of hemophilia B mice following intramuscular injection of AAV1 serotype vectors [J]. MOLECULAR THERAPY, 2001, 4 (03) : 217 - 222

[13] Induction of tolerance to human factor VIII in mice [J]. BLOOD, 2001, 97 (10) : 3311 - 3312

[14] Cloning of adeno-associated virus type 4 (AAV4) and generation of recombinant AAV4 particles [J]. JOURNAL OF VIROLOGY, 1997, 71 (09) : 6823 - 6833

[15] Cloning and characterization of adeno-associated virus type 5 [J]. JOURNAL OF VIROLOGY, 1999, 73 (02) : 1309 - 1319

[16] Conrad CK, 1996, GENE THER, V3, P658

[17] Recombinant adeno-associated virus type 2, 4, and 5 vectors: Transduction of variant cell types and regions in the mammalian central nervous system [J]. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 2000, 97 (07) : 3428 - 3432

[18] A new dual-vector approach to enhance recombinant adeno-associated virus-mediated gene expression through intermolecular cis activation [J]. NATURE MEDICINE, 2000, 6 (05) : 595 - 598

[19] Enhancement of muscle gene delivery with pseudotyped adeno-associated virus type 5 correlates with myoblast differentiation [J]. JOURNAL OF VIROLOGY, 2001, 75 (16) : 7662 - 7671

[20] Structural analysis of adeno-associated virus transduction circular intermediates [J]. VIROLOGY, 1999, 261 (01) : 8 - 14