[1] Harvard Univ, Sch Med, Beth Israel Deaconess Med Ctr, Dept Med, Boston, MA 02115 USA
[2] Childrens Hosp, Howard Hughes Med Inst, Boston, MA 02115 USA
[3] Ctr Blood Res, Boston, MA 02115 USA
[4] Harvard Univ, Sch Med, Dept Genet, Boston, MA 02115 USA