RANDOMIZED, DOUBLE-BLIND 6-MONTH TRIAL OF PREDNISONE IN DUCHENNES MUSCULAR-DYSTROPHY

被引:392
作者
MENDELL, JR
MOXLEY, RT
GRIGGS, RC
BROOKE, MH
FENICHEL, GM
MILLER, JP
KING, W
SIGNORE, L
PANDYA, S
FLORENCE, J
SCHIERBECKER, J
ROBISON, J
KAISER, K
MANDEL, S
ARFKEN, C
GILDER, B
机构
[1] UNIV ROCHESTER, ROCHESTER, NY 14627 USA
[2] STRONG MEM HOSP, ROCHESTER, NY 14642 USA
[3] IRENE JOHNSON INST REHABIL, ST LOUIS, MO USA
[4] WASHINGTON UNIV, DIV BIOSTAT, ST LOUIS, MO 63130 USA
[5] VANDERBILT UNIV, NASHVILLE, TN 37240 USA
关键词
D O I
10.1056/NEJM198906153202405
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:1592 / 1597
页数:6
相关论文
共 30 条
[21]   GLUCOCORTICOID-STIMULATED ACCUMULATION OF MOUSE MAMMARY-TUMOR VIRUS-RNA - INCREASED RATE OF SYNTHESIS OF VIRAL-RNA [J].
RINGOLD, GM ;
YAMAMOTO, KR ;
BISHOP, JM ;
VARMUS, HE .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1977, 74 (07) :2879-2883
[22]   STEROID-HORMONE REGULATION OF GENE-EXPRESSION [J].
RINGOLD, GM .
ANNUAL REVIEW OF PHARMACOLOGY AND TOXICOLOGY, 1985, 25 :529-566
[23]  
Seeman P M, 1966, Int Rev Neurobiol, V9, P145, DOI 10.1016/S0074-7742(08)60138-5
[24]  
SIEGEL IM, 1974, ILLINOIS MED J, V145, P32
[25]  
STRACHER A, 1982, MUSCLE NERVE, V5, P494
[26]  
WEISSMANN G, 1964, FED PROC, V23, P1038
[27]   IMMUNOCYTOCHEMICAL STUDIES OF CATHEPSIN-D IN HUMAN SKELETAL-MUSCLE [J].
WHITAKER, JN ;
BERTORINI, TE ;
MENDELL, JR .
ANNALS OF NEUROLOGY, 1983, 13 (02) :133-142
[28]   STEROID INDUCTION OF MOUSE MAMMARY-TUMOR VIRUS - EFFECT UPON SYNTHESIS AND DEGRADATION OF VIRAL-RNA [J].
YOUNG, HA ;
SHIH, TY ;
SCOLNICK, EM ;
PARKS, WP .
JOURNAL OF VIROLOGY, 1977, 21 (01) :139-146
[29]   THE DUCHENNE MUSCULAR-DYSTROPHY GENE-PRODUCT IS LOCALIZED IN SARCOLEMMA OF HUMAN SKELETAL-MUSCLE [J].
ZUBRZYCKAGAARN, EF ;
BULMAN, DE ;
KARPATI, G ;
BURGHES, AHM ;
BELFALL, B ;
KLAMUT, HJ ;
TALBOT, J ;
HODGES, RS ;
RAY, PN ;
WORTON, RG .
NATURE, 1988, 333 (6172) :466-469
[30]  
1988, SAS USERS GUIDE STAT, P549