Lethal toxicity, severe endothelial injury, and a threshold effect with high doses of an adenoviral vector in baboons

被引:142
作者
Morral, N
O'Neal, WK
Rice, K
Leland, MM
Piedra, PA
Aguilar-Córdova, E
Carey, KD
Beaudet, AL
Langston, C
机构
[1] Baylor Coll Med, Dept Mol & Human Genet, Houston, TX 77030 USA
[2] Baylor Coll Med, Dept Microbiol & Immunol, Houston, TX 77030 USA
[3] Baylor Coll Med, Dept Pediat, Houston, TX 77030 USA
[4] Baylor Coll Med, Dept Pathol, Houston, TX 77030 USA
[5] SW Fdn Biomed Res, San Antonio, TX 78227 USA
关键词
D O I
10.1089/10430340152712692
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
The effects of intravenous administration of a first-generation adenoviral vector expressing beta-galactosidase were compared in two baboons receiving a high dose or lower dose of vector, 1.2 x 10(13) or 1.2 x 10(12) particles/kg, respectively. The high-dose baboon developed acute symptoms, decreased platelet counts, and increased liver enzymes, and became moribund at 48 hr after injection, while the lower-dose baboon developed no symptoms. Expression of the beta-galactosidase transgene was prominent in liver, spleen, and endothelium of the arterial vasculature in the high-dose baboon, but was much more limited and spared the endothelium in the lower-dose baboon. Injury to the vascular endothelium was the most prominent abnormality in the high-dose baboon. Extensive histological studies provide a detailed picture of the pathology associated with a lethal dose of first-generation adenoviral vector in a primate.
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页码:143 / 154
页数:12
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